Learn about FDA-approved gene therapies from the Gene Therapy Program.
… adrenoleukodystrophy (CALD), but also highlight a risk for cancer. Read more FDA-approved gene therapy for Duchenne … body's T-cells to better detect and destroy infected or cancerous cells. It is also the first FDA-approved CAR … T-cell therapy. The Dana-Farber/Boston Children's Cancer and Blood Disorders Center is offering KYMRIAH® to …
… Kamihara , MD, PhD Physician, Dana-Farber/Boston Children's Cancer and Blood Disorders Center; Director, Pediatric Cancer Genetic Risk Program; Director of Medical Therapies, … Experimental Therapeutics, Dana-Farber/Boston Children's Cancer and Blood Disorders Center Associate Professor of …
Director, Harvard-wide Pediatric Health Services Research Fellowship; Director, Patient Safety Research Program
Associate Professor, Harvard Medical School
Kathleen E. Walsh, MD, MSc is a general pediatrician with clinical research fellowship training, including a Masters in Epidemiology. Her research focuses on patient safety, particularly the safe care of...
… , MD, MS Attending Physician, Dana-Farber/Boston Children's Cancer and Blood Disorders Center Instructor of Pediatrics, … Pediatric Nurse Practitioner, Dana-Farber/Boston Children's Cancer and Blood Disorders Center Image Emily Drake , BSN, … Image Eva Resto-Estrada Pediatric Program Coordinator, Cancer and Blood Disorders Center Meet Our Team …